Health Technology Assessment (HTA) DatabaseUsefulness of alpha-glucosidase in pompe disease
Pichon Riviere A, Augustovski F, Alcaraz A, Bardach A, Colantonio L, Ferrante D, Garcia Marti S, Glujovsky D, Lopez A, Regueiro A, Calcagno J I
| Record status | This is a bibliographic record of a published health technology assessment from a member of INAHTA. No evaluation of the quality of this assessment has been made for the HTA database. |
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| Bibliographic details | Pichon Riviere A, Augustovski F, Alcaraz A, Bardach A, Colantonio L, Ferrante D, Garcia Marti S, Glujovsky D, Lopez A, Regueiro A, Calcagno J I. Usefulness of alpha-glucosidase in pompe disease. Ciudad de Buenos Aires: Institute for Clinical Effectiveness and Health Policy (IECS) 2006
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| Authors' objectives | This report aims to assess the evidence available on the usefulness of substitutive enzymatic treatment with alpha-glucosidase for Pompe disease.
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| Authors' conclusions | Enzyme replacement with alpha-glucosidase has proved to improve survival in patients with Pompe disease, although trials with longer follow-ups are needed. The studies found were all case series reports, because of the disease low prevalence. It is the first treatment available to alter the course of Pompe disease. However, its annual cost is frequently prohibitive for many societies.
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| URL for original research | http://www.iecs.org.ar/ |
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| Subject index terms status | Subject indexing assigned by CRD |
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| Subject index terms | alpha-Glucosidases /therapeutic use; Costs and Cost Analysis |
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| Language | Spanish |
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| Address for correspondence | Viamonte 2146 - 3 Piso, C1056ABH Ciudad de Buenos Aires, Argentina, Tel: +54 11 49 66 00 82, Fax: +54 11 49 53 40 58
 info@iecs.org.ar |
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| English summary | English summary available |
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| Accession number | 32006001595 |
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| Database entry date | 19 December 2006 |
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© Copyright: Institute for Clinical Effectiveness and Health Policy (IECS)
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